What is the therapy of the human gene?

Therapy of the human gene is the technique of treatment of various diseases and disorders by replacing defective genes healthy. Gene therapy is performed at the cellular level, and most of them have been in the experimental stages since 2011. Normal genes work using proteins to perform certain coding sequences; When the gene is defective, the proteins cannot perform these instructions correctly. Using human gene therapy, scientists have tried to introduce healthy genes into specific cells by several different methods.

One type of gene therapy uses a modified virus as a carrier for a new, healthy gene. Scientists have developed techniques to change the natural way in which viruses give their pathogenic mass cells. Instead of mass causing infection, carrier viruses can insert normal human genes into targeted cells. This method has tried in pulmonary and liver cells to help cure the infections of these organs.

The treatment of the human gene may also be overlaid by methods that do not use viruses. Some scientists have tried to repair the origindays genes with a process called reverse mutation with mixed results. Different genes can be changed in different levels and scientists have also tried to manipulate these changes in these changes.

Some experiments in the human gene therapy were more successful when the defective gene is completely removed and replaced by a healthy gene. This technique is known as a gene exchange. Other studies of gene therapy had better results when the defective gene is left in place and with it is inserted normal. Factors affecting these results may include the type of target cell and the nature of the disorder treated.

The therapy of the disease gene had some success in the treatment of inherited conditions, such as haemophilia and a serious combined immune deficiency. The greatest challenge Wiping gene therapy for these conditions is the possibility of rejecting cells. If the patient's body recognizes cells with modified genes as foreign objects, the results may be life -threatening if he has teNto patient non -functional immune system.

Medical scientists continue to investigate the possibilities of using the human gene therapy for a wider range of conditions. Tests in the therapy of animal genes were effective in improving health problems such as degenerative blindness and even depression. Retinal genes introduced into cells of almost blind rats have successfully restored more of their supervision. A similar gene therapy in the mouse brains has restored the function of the key protein needed to alleviate severe clinical depression.